Refreshing results…
Delivery of oligonucleotide‐based therapeutics: challenges and opportunities
Download from doi.orgExon-skipping advances for Duchenne muscular dystrophy
UploadThe Use of Tricyclo-DNA Oligomers for the Treatment of Genetic Disorders
Download from doi.orgX chromosome inactivation in female patients with Fabry disease
Download from api.wiley.comUrinary biomarker investigation in children with Fabry disease using tandem mass spectrometry
Download from www.researchgate.netGlutamyl-tRNAGln amidotransferase is essential for mammalian mitochondrial translation in vivo
Download from portlandpress.comMissing publications? Search for publications with a matching author name.