Daniel Dever
0000-0001-5966-4803
5 papers found
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Development of β-globin gene correction in human hematopoietic stem cells as a potential durable treatment for sickle cell disease
Gene replacement of α-globin with β-globin restores hemoglobin balance in β-thalassemia-derived hematopoietic stem and progenitor cells
Cas9-AAV6 gene correction of beta-globin in autologous HSCs improves sickle cell disease erythropoiesis in mice
The TRACE-Seq method tracks recombination alleles and identifies clonal reconstitution dynamics of gene targeted human hematopoietic stem cells
Diamond Blackfan anemia is mediated by hyperactive Nemo-like kinase
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