Dissemin is shutting down on January 1st, 2025

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Massachusetts Medical Society, New England Journal of Medicine, 9(369), p. 819-829

DOI: 10.1056/nejmoa1208760

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Safety and efficacy of RNAi therapy for transthyretin amyloidosis.

This paper was not found in any repository, but could be made available legally by the author.
This paper was not found in any repository, but could be made available legally by the author.

Full text: Unavailable

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Preprint: archiving allowed
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Postprint: archiving allowed
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Data provided by SHERPA/RoMEO

Abstract

Transthyretin amyloidosis is caused by the deposition of hepatocyte-derived transthyretin amyloid in peripheral nerves and the heart. A therapeutic approach mediated by RNA interference (RNAi) could reduce the production of transthyretin.