Splice-Switching Antisense Oligonucleotides Correct Phenylalanine Hydroxylase Exon 11 Skipping Defects and Rescue Enzyme Activity in Phenylketonuria
Journal article published in 2024 by
Ainhoa Martínez-Pizarro,
Mar Álvarez,
Maja Dembic,
Caroline A. Lindegaard,
Margarita Castro,
Eva Richard,
Brage S. Andresen,
Lourdes R. Desviat 
This paper was not found in any repository, but could be made available legally by the author.
Full text: Unavailable
Published version:
archiving forbidden
Data provided by 