Gonçalves M., Matos L., Santos J.I., Coutinho M.F., Prata M.J., Pires M.J., Oliveira P., Alves S. Mutation-adapted U1snRNA as a therapeutic strategy for Mucopolysaccharidosis IIIC: in vitro and in vivo studies (2021) XIII Genetics and Biotechnology Journeys (online). Oral com.
Published in 2021 by
S. Alves 
