Gonçalves M, Matos L, Santos JI, Coutinho MF, Prata MJ, Pires MJ, Oliveira PA, Alves S. Mutation-adapted U1 snRNA as a therapeutic strategy for Mucopolysaccharidosis IIIC: in vitro and in vivo studies. 52nd Portuguese Society of Phamacology (SFF) meeting. Porto, Portugal. February, 2022. Oral com.
Published in 2022 by
Sandra Alves 
