Expert recommendations and clinical considerations in the use of onasemnogene abeparvovec gene therapy for spinal muscular atrophy
Journal article published in 2021 by
Elizabeth A. Kichula,
Crystal M. Proud,
Michelle A. Farrar,
Jennifer M. Kwon,
Kayoko Saito,
Isabelle Desguerre,
Hugh J. McMillan 
This paper is made freely available by the publisher.
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