Published in
American Association for the Advancement of Science, Science Translational Medicine, 573(12), 2020
DOI: 10.1126/scitranslmed.aaz7423
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Bilateral visual improvement with unilateral gene therapy injection for Leber hereditary optic neuropathy
Journal article published in 2020 by
Patrick Yu-Wai-Man 
,
Nancy J. Newman,
Valerio Carelli ,
Mark L. Moster,
Valerie Biousse,
Alfredo A. Sadun,
Thomas Klopstock ,
Catherine Vignal-Clermont ,
Robert C. Sergott ,
Günther Rudolph ,
Chiara La Morgia ,
Rustum Karanjia,
Magali Taiel,
Laure Blouin,
Pierre Burguière
and other authors.
,
Nancy J. Newman,
Valerio Carelli ,
Mark L. Moster,
Valerie Biousse,
Alfredo A. Sadun,
Thomas Klopstock ,
Catherine Vignal-Clermont ,
Robert C. Sergott ,
Günther Rudolph ,
Chiara La Morgia ,
Rustum Karanjia,
Magali Taiel,
Laure Blouin,
Pierre Burguière
and other authors.
This paper was not found in any repository, but could be made available legally by the author.
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Abstract
At 96 weeks after unilateral intravitreal injection of rAAV2/2- ND4 , vision improved in both eyes in 78% of subjects affected with LHON.