Published in
American Association for the Advancement of Science, Science Translational Medicine, 572(12), 2020
DOI: 10.1126/scitranslmed.abb5413
Links
Tools
Slowing late infantile Batten disease by direct brain parenchymal administration of a rh.10 adeno-associated virus expressing CLN2
Journal article published in 2020 by
Dolan Sondhi 
,
Stephen M. Kaminsky,
Neil R. Hackett,
Odelya E. Pagovich,
Jonathan B. Rosenberg,
Bishnu P. De,
Alvin Chen,
Benjamin Van de Graaf,
Jason G. Mezey,
Grace W. Mammen,
Denesy Mancenido,
Fang Xu,
Barry Kosofsky,
Kaleb Yohay ,
Stefan Worgall
and other authors.
,
Stephen M. Kaminsky,
Neil R. Hackett,
Odelya E. Pagovich,
Jonathan B. Rosenberg,
Bishnu P. De,
Alvin Chen,
Benjamin Van de Graaf,
Jason G. Mezey,
Grace W. Mammen,
Denesy Mancenido,
Fang Xu,
Barry Kosofsky,
Kaleb Yohay ,
Stefan Worgall
and other authors.
This paper was not found in any repository, but could be made available legally by the author.
Full text: Unavailable
Published version:
archiving forbidden
Data provided by 
Abstract
Administration of an adeno-associated virus coding for the CLN2 gene into the brain parenchyma slows the progression of CLN2 disease in children.