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Wiley, Journal of Inherited Metabolic Disease, 6(38), p. 1129-1136

DOI: 10.1007/s10545-015-9845-5

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A prospective 10-year study of individualized, intensified enzyme replacement therapy in advanced Fabry disease

Journal article published in 2015 by Raphael Schiffmann, Caren Swift, Xuan Wang, Derek Blankenship, Markus Ries
This paper is available in a repository.
This paper is available in a repository.

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